09-26-2021 / At St. Jude Children’s Hospital, scientists used an integrated sequencing platform to understand genomic variants associated with a broad range of pediatric cancer types.

09-13-2021 / Learn about a new CRISPR/Cas9 application leveraging its RNA guided specificity to self-assemble peptide fused and inactivated Cas9 onto DNA microarrays.

08-30-2021 / Learn how AAV2-hAADC gene therapy targeting dopamine neurons in the midbrain allowed restoring motor function in AADC patients.

08-16-2021 / Learn how lentiviral vectors promise to offer a safer gene delivery approach for correction of immunological deficits in SCID-ADA.

08-02-2021 / Learn how an influenza hemagglutinin nanoparticle vaccine protects against influenza viral strains by inducing broad neutralizing antibodies.

07-19-2021 / Learn how structure-guided modifications to CRISPR/Cas12a and Cas9 in the Kleinstiver lab have expanded access to genome sequences by expanding PAM preferences.

07-15-2021 / The Porteus lab is developing gene editing strategies to correct disease causing mutations. His lab focuses on modifying stem cells through the combined use of CRISPR/Cas9 gene editing tools and AAV vectors for payload delivery. Following ex vivo

07-06-2021 / Inherited retinal diseases are due to mutations in a broad range of genes leading to partial or total vision loss. Learn how genes are delivered for therapy.

06-08-2021 / Genetically engineered immune cells have gained attention as they have become an increasingly effective approach against some cancer types